Treatment with salanersen slowed neurodegeneration and improved motor function in children with SMA in a Phase 1 trial, ...

Living with SMA isn't just about survival, says columnist. There's also the emotional weight of preparing for the next crisis ...

Buckle up, it's going to be an incredible ride, columnist Helen Baldwin says in a letter to her 13-year-old self.

Earlier this month, I took a trip to England with my dad and my friend Anna — my first overseas adventure. I’m posting my photos on my Instagram account (you have to follow me to see them) and will be ...